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A call for global action for rare diseases in Africa 

Gareth S. Baynam, Stephen Groft, Francois H. van der Westhuizen, Safiyya D. Gassman, Kelly du Plessis, Emily P. Coles, Eda Selebatso, Moses Selebatso, Boikobo Gaobinelwe, Tebogo Selebatso, Dipesalema Joel, Virginia A. Llera, Barend C. Vorster, Barbara Wuebbels, Benjamin Djoudalbaye, Christopher P. Austin, Judit Kumuthini, John Forman, Petra Kaufmann, James Chipeta, Désirée Gavhed, Annika Larsson, Maja Stojiljkovic, Ann Nordgren, Emilio J. A. Roldan, Domenica Taruscio, Durhane Wong-Rieger, Kristen Nowak, Gemma A. Bilkey, Simon Easteal, Sarah Bowdin, Juergen K. V. Reichardt, Sergi Beltran, Kenjiro Kosaki, Clara D. M. van Karnebeek, Mengchun Gong, Zhang Shuyang, Ruty Mehrian-Shai, David R. Adams, Ratna D. Puri, Feng Zhang, Nicholas Pachter, Maximilian Muenke, Christoffer Nellaker, William A. Gahl, Helene Cederroth, Stephanie Broley, Maryke Schoonen, Kym M. Boycott and Manuel Posada (Nature Research, 2019-12-23)
The 11th International Conference on Rare Diseases and Orphan Drugs (ICORD), South Africa, included the Africa-Rare initiative launch and facilitated multi-stakeholder engagement in the challenges facing, and opportunities ...

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Author
Gareth S. Baynam, Stephen Groft, Francois H. van der Westhuizen, Safiyya D. Gassman, Kelly du Plessis, Emily P. Coles, Eda Selebatso, Moses Selebatso, Boikobo Gaobinelwe, Tebogo Selebatso, Dipesalema Joel, Virginia A. Llera, Barend C. Vorster, Barbara Wuebbels, Benjamin Djoudalbaye, Christopher P. Austin, Judit Kumuthini, John Forman, Petra Kaufmann, James Chipeta, Désirée Gavhed, Annika Larsson, Maja Stojiljkovic, Ann Nordgren, Emilio J. A. Roldan, Domenica Taruscio, Durhane Wong-Rieger, Kristen Nowak, Gemma A. Bilkey, Simon Easteal, Sarah Bowdin, Juergen K. V. Reichardt, Sergi Beltran, Kenjiro Kosaki, Clara D. M. van Karnebeek, Mengchun Gong, Zhang Shuyang, Ruty Mehrian-Shai, David R. Adams, Ratna D. Puri, Feng Zhang, Nicholas Pachter, Maximilian Muenke, Christoffer Nellaker, William A. Gahl, Helene Cederroth, Stephanie Broley, Maryke Schoonen, Kym M. Boycott and Manuel Posada (1)
SubjectAfrica (1)Diseases (1)... View MoreDate Issued
2019 (1)
Has File(s)Yes (1)

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